Published August 11, 2022 | Version v1
Patent Open

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

  • 1. University of Chicago

Contributors

Patent applicant:

Description

Antisense polynucleotides and their use in pharmaceutical compositions to induce exon skipping in targeted exons of the gamma sarcoglycan gene are provided, along with methods of preventing or treating dystrophic diseases such as Limb-Girdle Muscular Dystrophy.

Files

US20220251559.pdf

Files (6.4 MB)

Name Size Download all
md5:79d4c7e9697ae7f46b6b127d542606ce
6.4 MB Preview Download

Additional details

Identifiers

Patent application number
US 202217727376 A
Patent number
US 2022/0251559 A1
Other
oai:uchicago.tind.io:9068

Dates

Patent filed
2022-04-22

UChicago Information

Division(s)
Biological Sciences Division
Department(s)
Medicine