Published May 20, 2021
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ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
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Patent applicant:
Description
Antisense polynucleotides and their use in pharmaceutical compositions to induce exon skipping in targeted exons of the gamma sarcoglycan gene are provided, along with methods of preventing or treating dystrophic diseases such as Limb-Girdle Muscular Dystrophy.
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US20210147845.pdf
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Additional details
Identifiers
- Patent application number
- US 202117143847 A
- Patent number
- US 2021/0147845 A1
- Other
- oai:uchicago.tind.io:9066
Dates
- Patent filed
-
2021-01-07