Biological Sciences Division
Published June 27, 2019 | Version v1
Patent Open

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

Creators

  • 1. University of Chicago

Contributors

Patent applicant:

Description

Antisense polynucleotides and their use in pharmaceutical compositions to induce exon skipping in targeted exons of the gamma sarcoglycan gene are provided, along with methods of preventing or treating dystrophic diseases such as Limb-Girdle Muscular Dystrophy.

Files

US20190194659.pdf

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Additional details

Identifiers

Patent application number
US 201916295341 A
Patent number
US 2019/0194659 A1
Other
oai:uchicago.tind.io:9063

Dates

Patent filed
2019-03-07

UChicago Information

Division(s)
Biological Sciences Division
Department(s)
Medicine